Rare Diseases: Drugs

(asked on 16th October 2023) - View Source

Question to the Department of Health and Social Care:

To ask the Secretary of State for Health and Social Care, how many highly specialised technology evaluations of medicines for very rare diseases conducted by the National Institute for Health and Care Excellence resulted in (a) a positive recommendation, (b) an optimised recommendation, (c) a recommendation for managed access, (d) a negative recommendation and (e) termination in each financial year since 2018-19.


Answered by
Will Quince Portrait
Will Quince
This question was answered on 20th October 2023

The following table shows a breakdown of technologies appraised through the National Institute for Health and Care Excellence’s highly specialised technology process by financial year from 2018/19:

Financial Year

2018/19

2019/20

2020/21

2021/22

2022/23

Total

Recommended

1

4

2

4

4

15

Optimised

0

0

0

0

1

1

Not recommended

0

0

0

0

0

0

Total

1

4

2

4

5

16

Terminated

0

0

0

0

0

0

Reticulating Splines