Morquio Syndrome: Drugs

(asked on 10th September 2015) - View Source

Question to the Department of Health and Social Care:

To ask the Secretary of State for Health, when he expects NICE to announce its decision on approving the Vimizim form of elosulfase alfa.


Answered by
George Freeman Portrait
George Freeman
This question was answered on 15th September 2015

The National Institute for Health and Care Excellence (NICE) published further draft guidance on 2 September 2015 which recommends elosulphase alfa (Vimizim) for the treatment of mucopolysaccharidosis (type IVA)/Morquio syndrome, subject to certain conditions. Interested parties now have until 23 September to comment on NICE’s draft recommendation.

NICE now expects to publish its final guidance in January 2016.

This content was generated for your convenience by Parallel Parliament and does not form part of the official record.
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